CRISPR/Cas9 editing in human pluripotent stemcell-cardiomyocytes highlights arrhythmias, hypocontractility, and energy depletion as potential therapeutic targets for hypertrophic cardiomyopathy

Diogo Mosqueira, Ingra Mannhardt, Jamie R. Bhagwan, Katarzyna Lis-Slimak, Puspita Katili, Elizabeth Scott, Mustafa Hassan, Maksymilian Prondzynski, Stephen C. Harmer, Andrew Tinker, James G.W. Smith, Lucie Carrier, Philip M. Williams, Daniel Gaffney, Thomas Eschenhagen, Arne Hansen, Chris Denning

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Biochemistry, Genetics and Molecular Biology